The European Medicines Agency has recommended the use of Pfizer's gene therapy for a rare bleeding disorder called hemophilia ...
Pfizer (PFE) stock gains as lung cancer therapy, Lorbrena, shows promising results in reducing disease progression or death ...
But the head of the FDA’s CBER office didn’t tip where the agency stands on potentially broadening use of Sarepta’s Duchenne gene therapy Elevidys.
Ultragenyx is gearing up to take its glycogen storage disease (GSD) treatment to regulators next year after the gene therapy ...
Amgen on Tuesday secured the FDA’s green light for the first interchangeable biosimilar to AstraZeneca’s Soliris to treat two ...
Kendric Cromer is the first commercial patient to receive the groundbreaking treatment. Kendric Cromer, 12, is the first patient in the United States to undergo a newly approved gene therapy for ...
The U.S. Food and Drug Administration approved Moderna's respiratory syncytial virus (RSV) vaccine, the company announced on ...
Stimulants are typically the go-to option for doctors prescribing treatments for attention-deficit hyperactivity disorder (ADHD). But some ADHD patients do not respond adequately to stimulants or ...
The global cell and gene therapy market is experiencing significant growth, driven by technological advancements, increasing ...
Eli Lilly’s Retevmo (selpercatinib) has won an FDA accelerated approval to treat certain kids ages two and older with either advanced or metastatic medullary thyroid cancer (MTC) with a RET ...
When we think of smoking-related cancers, lung cancer usually comes to mind. But smoking is also a major driver for bladder cancer. Now, a new treatment has come to Philadelphia to help more ...
The drug is a potential treatment for biliary atresia in patients who have undergone surgery in which blocked bile ducts are bypassed to restore normal bile flow. The growth was driven by spending on ...